Mini-series – Realizing the potential of gene therapy: how do we pave the path to patient delivery and access?
Pfizer, ARM, Dolon
October 2024
While gene therapies offer the potentially groundbreaking opportunity to improve outcomes for individuals with rare and severe diseases, their adoption introduces distinct challenges for health systems that are currently tailored for more conventional medicines. As such, there is a significant opportunity to improve care delivery and increase patient access to current and future gene therapies.
Introduction: Gene therapy mini-series
In this four part series, explore the opportunities and best practices that relate to the following topics. Click below to access any paper of interest:
Promoting multi-stakeholder education to support access to gene therapy
Enhancing the delivery of gene therapy through specific care models: examining centers of excellence
Facilitating effective health technology assessment for gene therapy
Novel payment models to facilitate patient access to gene therapy