Categories for Dolon Institute

ISPOR Europe panel report: Pricing and reimbursement of multiple indication medicines: Can a balance be found between different stakeholder perspectives to optimise value and access for patients, while ensuring sustainable and affordable innovation?

This ISPOR Europe 2024 panel report explores pricing and reimbursement (P&R) of multiple medicines in Europe. Work has culminated from the panellists and audience of ~800 participants, where they discussed key challenges and forward-looking solutions for multi-indication products. The insights... View More

How might JCA impact orphan sustainability in Europe?

In recognition of Rare Disease Day 2025, we turn our attention to EU Joint Clinical Assessment (JCA), to explore the potential impact of JCA across three key dimensions important to sustaining investment and launch of new rare disease treatments in... View More

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Promoting multi-stakeholder education to support access to gene therapy

While gene therapies offer the potentially groundbreaking opportunity to improve outcomes for individuals with rare and severe diseases, their adoption introduces distinct challenges for health systems that are currently tailored for more conventional medicines. As such, there is a significant... View More

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Facilitating effective health technology assessment for gene therapy

While gene therapies offer the potentially groundbreaking opportunity to improve outcomes for individuals with rare and severe diseases, their adoption introduces distinct challenges for health systems that are currently tailored for more conventional medicines. As such, there is a significant... View More

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Novel payment models to facilitate patient access to gene therapy

While gene therapies offer the potentially groundbreaking opportunity to improve outcomes for individuals with rare and severe diseases, their adoption introduces distinct challenges for health systems that are currently tailored for more conventional medicines. As such, there is a significant... View More