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Are supplemental appraisal/reimbursement processes needed for rare disease treatments? An international comparison of country approaches

Nicod E, Whittal A, Drummond M, Facey K.
July 2020

Are supplemental appraisal/reimbursement processes needed for rare disease treatments? An international comparison of country approaches. Orphanet journal of rare diseases. 2020 Dec;15(1):1-4.